All results

33 results for randomized double blind placebo controlled study assess efficacy safety and

• 9001-303 (ENVISION)

  The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is…

  Ages

  N/A - N/A

  Sexes

  Male

• ATYR

  This randomized, double-blind, placebo matched to efzofitimod-controlled, study will evaluate the safety, tolerability, immunogenicity, pharmacokinetic (PK),…

  Ages

  18 Years - 75 Years

  Sexes

  All

• Adaptive COVID-19 Treatment Trial (ACTT)

  This study is an adaptive, randomized, double-blind, placebo-controlled trial to evaluate the safety and efficacy of novel therapeutic agents in hospitalized…

  Ages

  18 Years - 99 Years

  Sexes

  All

• Armata

  Phase 1b/2a, Randomized, Double-Blind, Placebo-Controlled, Multiple Ascending Dose Escalation Study of the Safety, Tolerability, and Efficacy of Intravenous AP…

  Ages

  18 Years - N/A

  Sexes

  All

• Atacicept in Subjects With IgA Nephropathy

  A Phase 3 Study with Atacicept in Subjects With IgA Nephropathy (ORIGIN 3) This is a multi-part study comprising of the original Phase 2b study (active, no…

  Ages

  18 Years - N/A

  Sexes

  All

• BOOST3

  BOOST3 is a randomized clinical trial to determine the comparative effectiveness of two strategies for monitoring and treating patients with traumatic brain…

  Ages

  14 Years - N/A

  Sexes

  All

• CC-90001 in Subjects With Idiopathic Pulmonary Fibrosis

  This is a Phase 2, multicenter, multinational, randomized, double-blind, placebo-controlled study evaluating the efficacy, safety, pharmacokinetics (PK),…

  Ages

  40 Years - N/A

  Sexes

  All

• CTD-TCNPC-301

  A prospective, randomized, double-blind, placebo controlled, multi-center therapeutic study for patients age 3 and older with confirmed diagnosis of Niemann…

  Ages

  3 Years - N/A

  Sexes

  All

• EMBARK

  The study will evaluate the safety and efficacy of gene transfer therapy in boys with DMD. It is a randomized, double-blind, placebo-controlled study. The…

  Ages

  4 Years - 7 Years

  Sexes

  Male

• Edgewise-201 (CANYON)

  A study of EDG-5506 in Becker muscular dystrophy (known as CANYON) and pivotal cohort (known as GRAND CANYON). The EDG-5506-201 CANYON study was expanded to…

  Ages

  12 Years - 50 Years

  Sexes

  Male