All results

3 results for randomized double blind placebo controlled study assess efficacy safety and

• Edgewise-201 (CANYON)

  A study of EDG-5506 in Becker muscular dystrophy (known as CANYON) and pivotal cohort (known as GRAND CANYON). The EDG-5506-201 CANYON study was expanded to…

  Ages

  12 Years - 50 Years

  Sexes

  Male

• 9001-303 (ENVISION)

  The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is…

  Ages

  N/A - N/A

  Sexes

  Male

• EMBARK

  The study will evaluate the safety and efficacy of gene transfer therapy in boys with DMD. It is a randomized, double-blind, placebo-controlled study. The…

  Ages

  4 Years - 7 Years

  Sexes

  Male