All results

12 results

• 9001-303 (ENVISION)

  The study will evaluate the safety and efficacy of delandistrogene moxeparvovec gene transfer therapy in non-ambulatory and ambulatory males with DMD. This is…

  Ages

  N/A - N/A

  Sexes

  Male

• APOL1 Long-term Kidney Transplantation Outcomes Network (APOLLO)

  The APOLLO study is being done in an attempt to improve outcomes after kidney transplantation and to improve the safety of living kidney donation based upon…

  Ages

  N/A - N/A

  Sexes

  All

• ATHN Transcends: A Natural History Study of Non-Neoplastic Hematologic Disorders

  In parallel with the growth of American Thrombosis and Hemostasis Network's (ATHN) clinical studies, the number of new therapies for all congenital and…

  Ages

  N/A - N/A

  Sexes

  All

• Bleomycin, Carboplatin, Etoposide, or Cisplatin in Pediatric and Adult Patients With Germ Cell Tumor

  This partially randomized phase III trial studies how well active surveillance, bleomycin, carboplatin, etoposide, or cisplatin work in treating pediatric and…

  Ages

  N/A - N/A

  Sexes

  All

• DJUS Registry

  A multi-center global registry to obtain post-market safety and efficacy data on Boston Scientific Ureteral and Urinary Diversion Stents Inclusion Criteria…

  Ages

  N/A - N/A

  Sexes

  All

• Fabry Disease Registry

  The Fabry Registry is an ongoing, international multi-center, strictly observational program that tracks the routine clinical outcomes for patients with Fabry…

  Ages

  N/A - N/A

  Sexes

  All

• GUARDIAN

  The primary objective of this study is to collect real-world clinical performance data to assess the clinical outcomes of patients receiving heart transplants…

  Ages

  N/A - N/A

  Sexes

  All

• Gaucher Disease Registry

  The ICGG Gaucher Registry is an ongoing, international multi-center, strictly observational program that tracks the routine clinical outcomes for patients with…

  Ages

  N/A - N/A

  Sexes

  All

• MPS I Disease Registry

  The Mucopolysaccharidosis I (MPS I) Registry is an ongoing, observational database that tracks the outcomes of patients with MPS I. The data collected by the…

  Ages

  N/A - N/A

  Sexes

  All

• PTC923-004 extension study

  The main purpose of this study is to evaluate the long-term safety of PTC923 in participants with phenylketonuria, and to evaluate the changes from baseline in…

  Ages

  N/A - N/A

  Sexes

  All