Charcot-Marie-Tooth disease: Research Studies

3 Related Result(s)

  1. A Study to Assess the Safety and Effectiveness of FLX-787 in Subjects With Charcot-Marie-Tooth Disease Experiencing Muscle Cramps (COMMIT)

    The purpose of this study is to determine how well an investigational product works to prevent, relieve, and reduce muscle cramps in patients with Charcot...

  2. Study of ACE-083 in Patients With Charcot-Marie-Tooth Disease

    This is a multicenter, phase 2 study to evaluate the safety, tolerability, pharmacodynamics (PD), efficacy, and pharmacokinetics (PK) of ACE-083 in patients...

  3. Assessing Long Term Safety and Tolerability of PXT3003 in Patients With Charcot-Marie-Tooth Disease Type 1A (PLEO-CMT-FU)

    PXT3003 is a rational design, fixed combination of low-dose (RS) baclofen, naltrexone hydrochloride and D-sorbitol. The use of PXT3003 in a multicenter,...